Batten disease is the name for a group of genetic disorders, also referred to as neuronal ceroid lipofuscinoses (NCLs). It affects both children and adults. There are 13 types of NCLs that fall under ...

There are three other main types of NCL, including two forms that begin earlier in childhood and a very rare form that strikes adults. The symptoms of these three types are similar to those caused by ...

Chauncey grew up on a farm in rural northern California. At 18 he ran away and saw the world with a backpack and a credit card, discovering that the true value of any point or mile is the experience ...

Amicus Therapeutics is moving on from an early-phase Batten disease program after follow-up data showed the therapy didn't stop the fatal nervous system disease from progressing long-term. The company ...

The U.S. Food and Drug Administration has approved Brineura (cerliponase alfa) to treat a specific form of Batten Disease, a condition that typically starts between 2 and 4 years of age. The newly ...

LINCOLN, Neb. (KOLN) — This weekend, hundreds of people gathered in Lincoln for a conference dealing with Batten Disease. It’s rare, it’s always deadly — and there is still no cure — affecting only a ...