The switch from fetal to adult hemoglobin expression in humans is related to the active repression of HbF expression by BCL11A. A self-inactivating lentivirus vector with a short hairpin RNA designed ...
Poster talk will present safety and efficacy data for ENaBL-T, a lentiviral vector for in vivo engineering of BCMA CAR T cells, which supported the first in vivo BCMA CAR-T cell therapy clinical trial ...