MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today announced that the first patient has been dosed in ...

Colin Farrell, 49, said his worst day on a film set was when he screwed up a line over 40 times while shooting in front of ...

At a farm in Loudoun County, a family turned personal tragedy into hope. Through therapeutic horseback riding, they’re ...

Ultragenyx reported third quarter revenue of $160 million, with Crysvita contributing $112 million (North America $57 million, Latin America and Turkey $47 million, Europe $8 million). Dojolvi ...

Detailed price information for Astrazeneca Plc ADR (AZN-Q) from The Globe and Mail including charting and trades.

Good morning, and welcome to Ionis Third Quarter 2025 Financial Results Conference Call. As a reminder, this call is being recorded. At this time, I would like to turn the conference over to Mr. Wade ...

Ultragenyx Pharmaceutical has dosed the first participant in Aurora, a study evaluating GTX-102 (apazunersen) for angelman ...

Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that the first patient has been dosed in the Aurora study (NCT07157254) evaluating the efficacy and safety of GTX-102 (apazunersen), an ...

Ultragenyx Pharmaceutical ( ($RARE) ) just unveiled an update. On October 30, 2025, Ultragenyx Pharmaceutical announced the dosing of the first ...

Mitch McKenny ran from Broken Hill to Newcastle to raise awareness for Angelman syndrome. Medical staff in Dubbo implored him to stop running when he began experiencing pain in his hip, but he would ...

Affected populations: The disorder is believed to affect somewhere between 1 in 12,000 and 1 in 24,000 people, although these ...